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Trial Summaries

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Trial

DIABETES TRIALS

Summary

(2010)

A synopsis of the purposes, parameters, and outcome evidence for the following trials: DCCT, DCCT/EDIC, UKPDS-33, UKPDS-34, Kumamoto, PROACTIVE, ACCORD, ADVANCE, RECORD, STENO, UGDP, VADT, UKPDS-80, FDPS, DPP, IDPP, Stop-NIDDM, XENDOS, DREAM-Rosi, DREAM-Rami, NAVIGATOR

Prevention Trials Summary (2008)

An overview of the following drug trials, which focused on the efficacy in preventing the onset of Diabetes Mellitus: XENDOS(Orlistat), DREAM(Rosiglitazone), DREAM(Ramipril), STOP-NIDDM(Acarbose), Diabetes Prevention Program(Metformin, Lifestyle Mods), IDPP, FDPS

ACCORD-ADVANCE

(2008)

Very brief comparison between the results of ACCORD (N. Americaglimepiride, metformin, rosiglitazone, insulin) and ADVANCE (Eur/Asia – gliclazide, metformin) trials, which aimed to show the clinical outcomes associated with aggressive lowering of blood glucose in T2DM.  A very good example of why, in terms of drug therapy, more is not always better.

ACCORD

(2008)

Original Article

An outline of the methodology and results of the ACCORD T2DM trial examining the outcomes (Primary = MI, stroke, CV death) of aggressive lowering of haemoglobin A1C, achieved with various oral hypoglycemics +/- insulin.  Trial halted early due to increased mortality in intervention group.

ACCORD LIPID & BLOOD PRESSURE

(2010)

This trial summary provides an overview of the blood pressure-lowering and lipid-lowering sub-trials of the ACCORD T2DM study.  While the main trial examining intensive glucose-lowering was halted early due to safety concerns, these two sub-trials were permitted to proceed to their conclusion.  The lipid-lowering arm compares open-label Simvastatin 20-40mg/day in combination with either masked fenofibrate or placebo at preventing a first occurrence of major CV events (non-fatal MI or stroke, death from CV causes) in patients with T2DM and at a high risk of CVD, over a mean period of 4.7 years.  The BP-lowering arm compared the effects of intensive therapy targeting (SBP≤120mmHg) vs. standard therapy targeting (SBP≤140mmHg) at preventing these same primary endpoints for the same duration.  Results of these two sub-studies again seem to emphasize that an aggressive approach to managing chronic diseases does not always translate into improved patient outcomes – another reminder that the target should suit the patient, not vice versa.

ADVANCE

(2008)

Summary of the findings of the ADVANCE T2DM trial that aimed to determine whether there are any outcome benefits (Primary = nephropathy, retinopathy, CV death, nonfatal MI/stroke) to intensive glucose control achieved by a gliclazide regimen as compared to a non-gliclazide regimen.

AVANDIA &

CV RISK

(2007)

A “pros vs. cons” approach to the growing body of evidence, including the Nissen, Wolski Meta-analysis (NEJM MAY 2007), linking rosiglitazone to an increased risk of MI and CV death.  Yet another illustration of the possible harm associated with intensive blood glucose-lowering therapy.

DREAM

(2007)

An analysis of the international DREAM trials, which focused on people with impaired fasting glucose or impaired glucose tolerance and are at low risk of CV events.   The study aimed to determine whether the use of rosiglitazone 8mg/day or ramipril 15mg/day showed any benefit in slowing the development and progression of diabetes in this demographic, when compared to a placebo.

GLARGINE & CANCER (2009)

This document offers an explanation of the concerns surrounding insulin glargine (Lantus), a long-acting synthetic insulin analogue.  It also presents the strengths and weaknesses of the studies linking this drug to cancer, and whether or not these new findings have relevance to the diabetic population as a whole. (Excerpted with permission from Rapid Rx July 10, 2009)

RECORD

(2009)

A non-inferiority trial whose purpose was to determine whether the addition of rosiglitazone(4-8mg/day) to a regimen already consisting of either metformin(≤2550mg/day) or a sulfonylurea(glyburide≤15mg/day; gliclazide≤240mg/day; glimepiride≤4mg/day) would show a benefit (Primary = CV death or CV hosp) over a regimen of metformin + a sulfonylurea.

Trial

HYPERTENSION TRIALS

Summary

(2003)

An outline of the purposes and findings of the following trials: AASK, ALLHAT, ALLHAT LLT, CALM, CAPPP, ELITE II, FACET, HOPE, HOT, IDNT, INSIGHT, IRMA II, LIFE, NORDIL, OPTIMAAL, PROGRESS, QUIET, RENAAL, SHEP, STOP-Hypertension 2, SYST-EUR, UKPDS, Val-HeFT

ACCOMPLISH

(2008)

To judge efficacy of ACE Inhibitor (Benazepril 20-40mg/day) + Amlodipine 5-10mg/day vs. Benazepril 20-40mg/day + Hydrochlorothiazide 12.5-25mg/day in preventing CV death, non-fatal MI, and stroke in high-risk hypertensive patients.

ACCORD LIPID & BLOOD PRESSURE

(2010)

This trial summary provides an overview of the blood pressure-lowering and lipid-lowering sub-trials of the ACCORD T2DM study.  While the main trial examining intensive glucose-lowering was halted early due to safety concerns, these two sub-trials were permitted to proceed to their conclusion.  The lipid-lowering arm compares open-label Simvastatin 20-40mg/day in combination with either masked fenofibrate or placebo at preventing a first occurrence of major CV events (non-fatal MI or stroke, death from CV causes) in patients with T2DM and at a high risk of CVD, over a mean period of 4.7 years.  The BP-lowering arm compared the effects of intensive therapy targeting (SBP≤120mmHg) vs. standard therapy targeting (SBP≤140mmHg) at preventing these same primary endpoints for the same duration.  Results of these two sub-studies again seem to emphasize that an aggressive approach to managing chronic diseases does not always translate into improved patient outcomes – another reminder that the target should suit the patient, not vice versa.

ALLHAT

(2003)

Designed to determine if there were any clinical outcome differences (Primary = non-fatal MI and fatal CHD) in high-risk hypertensive patients treated with relatively newer antihypertensive agents (amlodipine, lisinopril, doxazosin) versus a low-dose diuretic (chlorthalidone).

ANBP2

(2003)

Compares the findings of the ANBP2 trial (Australia) of ACE Inhibitors (enalapril) vs. diuretic (HCTZ) with those of the ALLHAT trial (N. America) and offers some possible insight as to why they are different.

ASCOT-BPLA

(2005)

Blood Pressure-Lowering Arm of ASCOT, to determine effect of amlodipine +/- perindopril vs. atenolol +/- bendroflumethiazide on ‘non-fatal MI and fatal CHD’ in moderate risk (eg. diabetes 27%) hypertensive patients without previous heart disease.

Summary

(2010 Members Only)

Updated and condensed summary of the following trials, including the “current knowledge” obtained from each: AASK, ALLHAT, ASCOT-BPLA, CALM, CAPPP, ELITE II, FACET, HOPE, HOT, IDNT, INSIGHT, IRMA II, LIFE, NORDIL, OPTIMAAL, PROGRESS, QUIET, RENAAL, SHEP, STOP-hypertension, SYST-EUR, UKPDS, Val-HeFT

Trial

LIPID-LOWERING TRIALS

SHARP

(2011)

 

Pattern of CVD changes as CKD progresses: early CKD cholesterol dependent atheromatous coronary disease; late CKD vascular calcification, LVH. Lipid lowering therapy (statin) is indicated to prevent atherosclerotic CVD in patients with CKD including those progressing to ESRD; findings emphasize need to treat early in disease process, however, point at which patients may no longer benefit remains unclear, and there is no evidence to support initiation of statin therapy in dialysis patients. Studies confirm that statin therapy is safe in late stage CKD. Role of ezetimibe is not clear, but unlikely to have contributed to clinical outcomes.

AIM-HIGH

(2011)

AIM-HIGH does NOT provide support for the use of ER niacin (NIASPAN) as an add on to statin therapy in a stable 2° prevention population already treated with ASA, beta-blockers, ACEi or ARB’s & statins. However likely was not designed appropriately to answer this question since ambitious estimated risk reduction, and early stop/short duration of the trial. Results for AIM-HIGH raise questions regarding modifiable nature of residual risk in patients reaching LDL targets on a statin.

Summary

(2004)

Provides a summary chart and general interpretation of the following lipid trials: 4S, PROVE-IT, HPS, WOSCOPS, ASCOT

ACCORD LIPID & BLOOD PRESSURE

(2010)

This trial summary provides an overview of the blood pressure-lowering and lipid-lowering sub-trials of the ACCORD T2DM study.  While the main trial examining intensive glucose-lowering was halted early due to safety concerns, these two sub-trials were permitted to proceed to their conclusion.  The lipid-lowering arm compares open-label Simvastatin 20-40mg/day in combination with either masked fenofibrate or placebo at preventing a first occurrence of major CV events (non-fatal MI or stroke, death from CV causes) in patients with T2DM and at a high risk of CVD, over a mean period of 4.7 years.  The BP-lowering arm compared the effects of intensive therapy targeting (SBP≤120mmHg) vs. standard therapy targeting (SBP≤140mmHg) at preventing these same primary endpoints for the same duration.  Results of these two sub-studies again seem to emphasize that an aggressive approach to managing chronic diseases does not always translate into improved patient outcomes – another reminder that the target should suit the patient, not vice versa.

ASCOT-LLA

(2003)

An overview of the ASCOT-LLA trial, which aimed to determine if there is any benefit to using atorvastatin(10mg/day)+antihypertensive meds vs. a placebo +antihypertensive meds in preventing clinical outcomes (Primary = fatal CHD, non-fatal MI) for high-risk hypertensive patients.

CARDS

(2004)

The CARDS trial was designed to judge the efficacy of atorvastatin(10mg/day) vs. a placebo in preventing CV disease outcomes (Primary = time to 1st occurrence of: CHD death, non-fatal MI (including silent), hospitalized for unstable angina, resuscitated cardiac arrest, coronary revascularization or stroke) for patients with T2DM and at least one other CVD risk factor.

ENHANCE

(2008)

This is a short(24 month) study comparing the effects of simvastatin(80mg/day) + ezetimibe(10mg/day) vs. simvastatin(80mg/day) + a placebo by using a surrogate marker (Primary = mean change in carotid artery intima-media thickness) in patients with elevated LDL levels and heterozygous familial hypercholesteremia.

IDEAL

(2006)

The IDEAL trial focuses on a comparison of high-dose atorvastatin(40-80mg/day) vs. low- to moderate-dose simvastatin(20-40mg/day).  It’s aim is to determine whether one regimen is superior to the other in preventing clinical outcomes (Primary = coronary death, non-fatal acute MI, or cardiac arrest with resuscitation) for patients with history of MI.

JUPITER

(2008)

An international trial that aimed to show the benefit of using rosuvastatin(20mg/day) vs. a placebo in preventing both clinical and surrogate outcomes (Primary = MI, stroke, arterial revascularization, hospitalization for unstable angina or death from CV causes) in low- to moderate-risk older adults with normal LDL and elevated C-reactive protein levels.

PROVE-IT

(2004)

PROVE-IT sought to examine the difference of efficacy in preventing hard clinical outcomes (Primary = all cause mortality, MI, unstable angina, revascularization, or stroke) between high-dose atorvastatin(80mg/day) vs. moderate-dose pravastatin(40mg/day) when either is added to the standard therapy for patients hospitalized with acute coronary syndrome.

SPARCL

(2006)

This study examines the benefit of using high-dose atorvastatin(80mg/day) vs. a placebo in preventing clinical outcomes (Primary = non-fatal or fatal stroke) for patients who have recently suffered a stroke or transient ischemic attack and have normal LDL and no known history of coronary heart disease.

Summary

(2010 Members Only)

A concise summary - including comparative graphs, primary/secondary endpoints, results, and brief analysis – of the following trials: 4S, LIPID, CARE, HPS, BIP, VA-HIT, CARDS, ASCOT, WOSCOPS, AFCAPS, HHS, WHO-CLOF.

 

Trial

ANTI-THROMBOTIC/ANTI-COAGULANT TRIALS

ACTIVE-A, ACTIVE-W

(2009)

The purpose of the ACTIVE-A trial was to determine whether Aspirin(75-100mg/day) + clopidogrel(75mg/day) is superior to Aspirin(75-100mg/day) + a placebo in preventing a composite of major vascular outcomes (Primary = stroke, non-CNS systemic embolism, MI, death from any cause) in patients with atrial fibrillation and at least one other risk factor for stroke (most pts had CHADS 1-2).  Of Note: Over the median 3.6 year follow-up, NNT=42 to prevent 1 stroke, NNH=42 to cause major bleeding.  The ACTIVE-W trial focuses on a similar patient demographic (most CHADS 2), but was designed to determine whether the combination of Aspirin(75-100mg/day) + clopidogrel(75mg/day) is superior to a Vit K antagonist (warfarin, titrate to INR 2-3) in preventing similar clinical outcomes.  ACTIVE-W trial halted early due to warfarin showing less harm and more benefit than the combo of Aspirin + clopidogrel.  Together, the ACTIVE trials make a strong case for the use of ASA only for low-risk patients and warfarin only for high-risk patients.

ARISTOTLE
(2011)

Apixiban vs warfarin in patients with Atrial Fibrillation.  In 18,201 patients over 1.8yrs with a CHADS2 score of ~2.1, apixapan was superior to warfarin, without the need for INR monitoring. Apixiban is not approved for use in Canada & there is no know antidote for this agent.

CHARISMA

(2006)

The CHARISMA trial was also concerned with the comparative efficacy of ASA(75-162mg/day) + clopidogrel(75mg/day) vs. ASA(75-162mg/day) + a placebo in preventing clinical outcomes (Primary = death from any cause, stroke) in patients at high-risk of atherosclerotic events and who have CVD or multiple CVD risk factors.  Of note: Over the 28 month follow-up, NNT=250 to prevent 1 stroke, while NNH=125 to cause moderate bleeding (safety endpoint).

CLOPIDOGREL-

PPI DI’s

(2009)

This document is a Q&A reflection on some of the recent evidence that shows a drug-interaction between clopidogrel (Plavix) and proton pump inhibitors, especially omeprazole and esomeprazole.  Included are sections offering the proposed mechanism(s) of this interaction, a discussion of the supporting evidence, and some tips on managing patients who may be at risk of this interaction.

RE-LY

(2010)

The RE-LY trial compares the benefits and risks over two years of Dabigatran 110mg BID or 150mg BID vs. dose-adjusted warfarin (INR 2-3) as long-term anticoagulant agents in patients with atrial fibrillation, who are also at increased risk of stroke.  Results of this trial show Dabigatran 110mg BID to be non-inferior vs. warfarin at preventing the primary endpoints (stroke or systemic embolism), while Dabigatran 150mg BID was shown to be both non-inferior and superior to warfarin at preventing these endpoints.  These benefits are accompanied by an increased frequency of dyspepsia in patients receiving either dose of Dabigatran, and the 150mg BID dose also showed a significantly higher frequency of GI bleeding.  However, patients receiving warfarin showed higher rates of life threatening, intracranial (the primary safety endpoint), and minor bleeding than patients receiving either dose of Dabigatran.  This summary aims to help the reader use the data provided by RE-LY to make practical choices that lead to the optimal drug therapy for each individual patient.

ROCKET-AF

(2011)

The ROCKET-AF trial sought to compare the novel anticoagulant Rivaroxaban 20mg OD (15mg in pts with CrCl=30-49µmol/L) vs. dose-adjusted warfarin (INR2-3) to reduce stroke or systemic embolism in high-risk patients (avg CHADS2=3.5) with persistent/paroxysmal atrial fibrillation.  Over the 1.9 year mean follow-up time, rivaroxaban was found to significantly reduce hemorrhagic stroke and systemic embolism, with lower rates of intracranial/critical/fatal bleeding compared with warfarin.  However, rivaroxaban showed increased rates of GI bleed, Hgb decline (≥20g/L), hematuria, and nosebleeds.  The trial was designed to assess outcomes using both intention-to-treat as well as per protocol analysis, allowing rivaroxaban to be compared with warfarin for both non-inferiority as well as superiority.  While rivaroxaban was shown to be non-inferior compared to warfarin for the primary endpoint, the data did not reach significance for superiority.  While the results of the trial are promising, the high cost (~$560/month) and lack of both an antidote as well as long-term safety data for this new agent seem to indicate that warfarin will still have a place in therapy for the foreseeable future.

Summary

(2010 Members Only)

A link to our latest “Oral Antiplatelet & Antithrombotic Agents” chart from the newly released 8th Edition Drug Comparison Chart Book (May 2010).  Includes most common therapeutic options and their indications, as well as detailed info on dosing, side effects, contraindications, and so much more!

Trial

HEART FAILURE TRIALS

ATLAS

(1998)

A brief summary of the results from the international ATLAS trial, which sought to distinguish whether an ACE-inhibitor (lisinopril) was more effective at low doses (2.5-5mg/day) or high doses (32.5-35mg/day) in preventing clinical outcomes (Primary = death from any cause) for patients with NYHA Class II-IV congestive heart failure.

CHARM

(2003)

The CHARM set of trials are designed to determine whether the use of an Angiotensin Receptor Blocker (candesartan ~24mg/day) along with standard therapy could prevent clinical outcomes (Primary = death from all causes) in patients with heart failure.  CHARM-Alternative focuses on the use of ARB’s in patients that are intolerant of ACE-inhibitors.  The CHARM Added wing of the study attempts to show a benefit to using ARB’s in addition to ACE-inhibitors in patients with heart failure.  Lastly, the CHARM Preserved arm examines whether there is any benefit to using ARB’s in patients with preserved left-ventricular function

Trial

HORMONE REPLACEMENT THERAPY

WHI, HERS, HERS II

(2002)

A findings summary for the WHI (Women’s Health Initiative) trials, which aims to determine the long-term effects of conjugated equine estrogen (Premarin, 0.625mg/day) + medroxyprogesterone (Provera, 2.5mg/day) in otherwise older, healthy postmenopausal women.  WHI focuses on clinical outcomes (Primary = CHD, invasive breast cancer) to weigh the benefits and drawbacks of combination HRT.  The summary also references several findings of the similar HERS/HERS II study, which focused on patients who already had CHD.  All three studies trend toward the same conclusion – the risks of long-term HRT may in fact outweigh the benefits in many postmenopausal women.  Finally, a chart is included that describes various approaches to HRT and the evidence (or lack thereof) supporting each, followed by a sampling of alternative therapeutic options to alleviate symptoms and risk factors common to postmenopausal women.  WHI trial halted early due to risk-benefit imbalance.

WHI and Age

(2002)

A further breakdown of the WHI trial findings, paying particular attention to how the age of trial participants may influence an interpretation of the results.  Also included is a discussion as to why an apparently small increase in breast cancer incidence from HRT must be weighed against other factors to gain a full appreciation of risk vs. benefit.

WHI Extras

(2002)

Yet another analysis of the data provided by the WHI trials, focusing on the primary study outcomes (CHD, invasive breast cancer) that eventually led to the early termination of the experiment.  Also includes a useful “Tips in Interpreting Data” section that can (and should!) be applied to any study.

Trials

ANEMIA TRIALS

Summary

(2010)

Provides a brief outline of the various etiologies resulting in anemia, followed by a summary of the intervention, population, and results of the following studies:

  Iron TrialsCharytan et al, Van Wyck et al, DeVita et al, Besarab et al, Macdougall et al, Fishbane et al, DRIVE-I, DRIVE-II

  ESA TrialsRevicki et al, Levin et al, CREATE, CHOIR, Canadian EPO Study Group, Parfrey et al, Foley et al, Besarab, Tonelli et al, TREAT

Also offers points to consider for both Iron and ESA therapy of chronic kidney disease, either with or without dialysis

Trials

ASTHMA TRIALS

Summary

(2006)

Offers an overview, with interpretive comments, of the population, intervention, and results for the following trials: SMART, Wolfe, Rabe, STAY, GOAL, Concept, Overbeek, START, Ram, Gibson, Ni, Adams(Cochrane), Lasserson(Cochrane), Masoli(Fluticasone), Masoli(Budesonide), IMPACT

Trial

MISCELLANEOUS TRIALS

CATIE-AD
(2011)

This trial compares the effectiveness of atypical antipsychotics drugs ( risperidone, quetiapine & olanzapine to placebo) in 421 patients for up to 36 weeks. There was no significant differences between any atypical agents & placebo for overall rate of discontinuation.  These agents offer limited efficacy, but differ in their side effect profile.

COX-2

INHIBITORS

(2001)

Summary of several studies that looked at the efficacy of various COX-2 inhibitors, including:

MELISSAMeloxicam(7.5mg/day) vs. Diclofenac(100mg SR/day)

SELECTMeloxicam(7.5mg/day) vs. Piroxicam(20mg/day)

CLASSCelecoxib(800mg/day) vs. Ibuprofen(2400mg/day) vs. Diclofenac(150mg/day)

→ Each class treatment arm was separated into two subgroups, one receiving ASA(≤325mg/day) and one receiving no ASA

VIGORRofecoxib*(50mg/day) vs. Naproxen(1000mg/day)     

OAB

(2008)

This trial summary looks at a study (Kay et al.) comparing Darifenacin(7.5-15mg/day) vs. Oxybutynin(10-20mg/day) vs. a placebo in improving memory recall outcomes (Primary = Name-Face Association Test score) for otherwise healthy older patients.  The main purpose of the study was to justify the use of Darifenacin over oxybutynin to treat urinary incontinence based on the newer drug’s improved side-effect profile (lower cognitive impairment).  This document also offers some insight into why the limitations of this study design prevent such a definitive justification.

Pain Control in Elderly Arthiritis (2011)

As a supplement to our newsletter, Q&A summary, and CFP article on opioid use for chronic non-cancer pain, this trial summary provides an overview of a recent observational cohort study examining the relative efficacy and safety of NSAID’s, Coxib’s, and opioids in elderly patients (84% women) with arthritis and <2 comorbidities.  The article offers some advice toward individualizing therapy for this difficult condition, and gives some interpretation of some of the more ambiguous data presented in the article.  Notably, a comment on the clinical significance of increased rates for CV events, mortality, fracture, and GI obstruction within the opioid cohort, and which of these adverse events should be of primary concern to caregivers.

Varenicline & Increased CV Risk

(2011)

In July 2011 there was a meta-analysis published in the CMAJ attributing an increased risk of serious cardiovascular events to varenicline (CHAMPIX in Canada), which is considered one of the more effective agents available for smoking cessation.  While the study authors rightly assert that their findings indicate a need to reassess the safety profile of varenicline, there has much debate (ex. AAFP, BMJ) as to whether their data is as broadly applicable as they claim.  This article seeks to clarify some of the issues being discussed in regard to varenicline, in order to put forward a slightly more nuanced interpretation of the original data.  Ultimately, it shows that even in the supposed hard science of evidence-based medicine, a NNT can still be a hotly debated subject.

Vick’s Vapor Rub for Cough & Cold (2011)

With Health Canada’s recent recommendation towards more conservative use of OTC cough & cold products in pediatrics, many parents have been left to wonder what they can do to try to relieve these symptoms in their children.  This summary focuses on a trial comparing topical Vapor Rub vs. white petrolatum vs. no treatment for the relief of night-time cough and cold symptoms in kids aged 2-11.  While the study itself is somewhat methodologically limited in the strength of evidence it provides, this article offers some context as to the overall efficacy of treatment with Vapor Rub, and how it fits into cough and cold management.  One interesting stat of note – Vapor Rub was slightly more likely to help the parents of sick children sleep through the night than it was their symptomatic kids – perhaps offering some insight into Health Canada’s more restrictive policies regarding the use of cough and cold products in this age group.

* Note: Rofecoxib withdrawn from market in 2004 due to increased CV risk